Some types of sickle cell disease cause severe illness, while others have a mild or unapparent course. Sickle cell disease is present from birth and inherited from genes you receive from your parents.
Agios collapsed ~50% in a single day after its pivotal RISE UP sickle cell disease, SCD trial delivered a split verdict: it met the hemoglobin (Hb) response endpoint but failed to show a statistically ...
Cristina Pina receives funding from Children's Cancer and Leukaemia Group via the Little Princess Trust and the National Centre for the Replacement, Reduction and Refinement of Animals in Research.
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback