Translating Next-Generation Science Into Transformative Gene Therapies Learn About Our Programs

Programs Encoded is building an internally developed pipeline of best- and potentially first-in-class therapies focused on neurological disorders.

Press Releases January 12, 2026 Encoded Therapeutics Announces U.S. FDA Breakthrough Therapy Designation Granted to ETX101 for the Treatment of Dravet Syndrome January 08, 2026 Encoded …

Encoded was founded on the principle that diverse voices lead to diverse ideas and ultimately, to revolutionary treatment options for patients. Our diversity – whether gender, ethnicity, sexual …

Encoded will be providing additional updates on its research pipeline, which is focused on both rare genetic and common disease programs, in addition to clinical progress with ETX101 for Dravet …

Contact Directory Patients Community and Clinical Trials [email protected] Healthcare Providers [email protected] Media [email protected] Finance/Accounting …

Encoded’s innovative AAV-mediated miRNA platform offers a promising strategy for long-term knockdown of target genes in the central and peripheral nervous systems.

Ever wondered what it takes to make a gene therapy? Join us on a virtual lab tour at Encoded’s headquarters in South San Francisco. Meet a few of our talented scientists ready to explain what …

5 days ago · Encoded is advancing a pipeline of programs across genetic epilepsies and other neurological disorders with significant unmet need. With integrated discovery, development, and …

Dec 16, 2025 · Encoded Therapeutics is a clinical-stage genetic medicines company developing one-time therapies for severe neurological disorders. Our vector engineering platform enables highly …